Rojas-Caro, S.Baric, I.Camarena Grande, C.Coker, M.Deegan, P.DiRocco, M.Ezgu, F. S.Feillet, F.Malinova, V.Mengel, E.Murphy, E.Pastor Rosado, J.Rahman, Y.Scarpa, M.Schwab, K. O.Smolka, V.Taybert, J.Valayannopoulos, V.Yang, Y.Quinn, A.2019-10-272019-10-2720150168-82781600-0641https://doi.org/10.1016/S0168-8278(15)31407-0https://hdl.handle.net/11454/4036450th International Liver Congress of the European-Association-for-the-Study-of-the-Liver -- APR 22-26, 2015 -- Vienna, AUSTRIAen10.1016/S0168-8278(15)31407-0info:eu-repo/semantics/closedAccessEFFICACY AND SAFETY OF SEBELIPASE ALFA IN CHILDREN AND ADULTS WITH LYSOSOMAL ACID LIPASE DEFICIENCY: RESULTS OF A PHASE 3 TRIALConference Object62S811S811WOS:000362830900402Q1